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Duchenne muscular dystrophy: promising early-stage clinical trials to watch
Personal take on this article: Duchenne muscular dystrophy (DMD) is a serious condition without a cure. Instead, treatments aim to slow down its progression. Currently, there are experimental treatments in phase I trials that could offer new options for patients. This review discusses ongoing and recent early-stage trials for DMD treatments. These include therapies that skip certain genetic sections (exons) and gene therapies. Additionally, it covers phase …