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Recent Progress in Gene-Targeting Therapies for Spinal Muscular Atrophy: Promises and Challenges
Personal take on this article: The article titled "Recent Progress in Gene-Targeting Therapies for Spinal Muscular Atrophy: Promises and Challenges" is a detailed review of the current advancements in gene-targeting treatments for Spinal Muscular Atrophy (SMA), a severe genetic disorder that leads to the loss of motor neurons, causing muscle weakness, loss of mobility, and potentially death if untreated. Key points: 1. SMA Overview: SMA is caused …