This study introduces the BMX mouse model for Becker muscular dystrophy, providing a new tool for studying disease mechanisms and testing potential therapies.
This study examines dystrophin and dystroglycan protein turnover after exon skipping therapy in DMD, highlighting protein stability changes and implications for gene correction strategies.
This study explores the potential of membrane stabilization therapy for LGMD2B using vamorolone, showing it outperforms prednisolone in muscle repair and strength restoration.